Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to a unique genetic mutation to save an infant named Baby KJ from dying of a ...

At Mayo Clinic, cardiologists Peter Noseworthy, M.D., and John Giudicessi, M.D., Ph.D., are uncovering the earliest signs of ...

Penn and CHOP researchers want to develop urea cycle disorder treatments using CRISPR gene-editing therapy. Get unlimited access to Inquirer.com and The Inquirer App, plus 5 articles each month to ...

GATC brought together a broad coalition of researchers and executives in cell and gene therapy, gene editing, drug discovery and AI as well as patients and advocates.

The research will support the implementation of precision medicine efforts for the population. Read more at straitstimes.com. Read more at straitstimes.com.

New research reveals insomnia's deep links to cardiovascular health, urging us to treat it as a core medical issue, not a ...

An estimated 6.7 million Americans over the age of 65 live with Alzheimer’s, so it's important to know the early signs of ...

Personalized cancer treatments have the potential to transform and extend the life of millions, but the region’s healthcare ...

The EMA’s recommendation follows evidence that the targeted therapy improves progression-free survival in patients whose ...

Amyotrophic lateral sclerosis (ALS) is a rare, rapidly progressive neurodegenerative disease with devastating clinical and ...