Angelman syndrome affects roughly 1 in every 20,000 children and it has no approved treatment. Researchers recently published results of early tests of a gene therapy strategy for Angelman syndrome, a ...

For the first time, Colin Farrell has opened up his home and talked in-depth about life with his son James, who has Angelman syndrome. James was just a toddler when he was diagnosed with the rare ...

Angelman syndrome is a rare disease that disrupts the normal development and function of cells, particularly in the nervous system, leading to severe developmental delays and learning disabilities.

CHAPEL HILL – Scientists at the UNC School of Medicine have reported in the journal JCI Insight encouraging early tests of a gene therapy strategy against Angelman syndrome, a neurodevelopmental ...

Meghan Edberg is the mother of five-year-old named William. About three years ago, when William was nonverbal and started exhibiting developmental delay, genetic testing confirmed that he had Angelman ...

Actor Colin Farrell has opened up about the difficult decision to move his son James, who has Angelman syndrome, into a long-term care facility. In an interview this week the actor, 48, revealed he ...

NOVATO, Calif., Oct. 30, 2025 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today announced that the first patient has been dosed in the Aurora study (NCT07157254) evaluating the ...

MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today announced that the first patient has been dosed in ...

Colin Farrell is honoring his son by starting a new foundation to help people with intellectual disabilities. The Oscar-nominated actor, 48, has launched the Colin Farrell Foundation, which is ...